What are the potential benefits and risks of gene editing technologies for treating inherited muscle atrophies?

Multiple system atrophy (MSA), formerly called Shy-Drager syndrome, is a rare condition of the brain and nervous system. MSA affects the body's ability to ... Spinal muscular atrophy (SMA) attacks motor nerve cells in the spinal cord, taking away a child's ability to walk, eat, or breathe. Spinal muscular atrophy is ... If you are found to be a carrier for SMA, your partner should undergo carrier testing as well. If your partner's test is negative, the chance to have an ... It's sometimes called Werdnig-Hoffmann disease or infantile-onset SMA. Children with type 1 have limited movement, can't sit without support, and have trouble ... Jan 12, 2021 ... Excessive muscle loss is a bad prognostic index of a variety of diseases ranging from cancer, organ failure, infections and unhealthy ageing. Dec 31, 2024 ... Optic atrophy is a condition in which the optic nerve begins to deteriorate. The optic nerve is the nerve at the back of your eye that connects your eye to ... Background:The presentation of symptoms for multiple system atrophy (MSA) varies. Because there are no specific markers for its clinical diagnosis, the. More videos on YouTube ... Posterior cortical atrophy (PCA), also called Benson's syndrome, is a rare, visual variant of Alzheimer's disease. It affects areas in ... Posterior cortical atrophy ... Posterior cortical atrophy, also known as PCA, is an uncommon type of dementia that usually begins by affecting a person's vision. Spinal Muscular Atrophy Risk Factors. Spinal muscular atrophy affects between 10,000 and 25,000 children and adults in the U.S. and approximately one in every ...